Innovation in Gene Therapy Starts at UPMC Children’s

UPMC Children’s is on its way to becoming the lead site for development and human clinical trials of a new gene therapy treatment for VLCADD (Very Long Chain Acyl CoA Dehydrogenase Deficiency), a rare genetic disorder that is identified through newborn screening.
UPMC Children’s Hospital Foundation Receives $1 Million Gift from Alba Tull to Benefit Children’s Neuroscience Institute

In April 2022, UPMC Children’s Hospital Foundation received a $1 million gift from Alba Tull to advance pediatric neuroscience research, education and patient care at UPMC Children’s Hospital of Pittsburgh’s Children’s Neuroscience Institute (CNI).
Lasting Gifts to Strengthen Music Therapy at UPMC Children’s

Music therapy is one of UPMC Children’s most treasured programs.
Ninth Grade Athlete and Heart Transplant Recipient Organizes Golf Fundraiser

Owen and his community organized a fundraising golf event, which he called “Golf FORE Heart.”
Blazing New Trails in Transplantation

UPMC Children’s is at the forefront of pediatric transplantation research.